Developing novel small-molecule
therapeutics for rare pediatric diseases

Rapidly advancing drug discovery
for genetically-defined rare diseases

NOBIAS THERAPEUTICS is a clinical-stage company developing novel small-molecule therapeutics for rare diseases. Our unique access to rich genomic and health datasets and strong relationships with pediatric academic medical centers across North America allow us to rapidly advance drug discovery for genetically-defined rare diseases, with an initial focus on pediatric indications, but expansion opportunities in adults and non-rare indications.